Abeona Therapeutics

abeonatherapeutics.com

Abeona Therapeutics Inc. is a clinical-stage biopharmaceutical company developing cell and gene therapies for serious diseases. Prademagene Zamikeracel (PZ-Cel) is Abeona’s investigational autologous, COL7A1 gene-corrected epidermal sheets currently in development for recessive dystrophic epidermolysis bullosa. The company’s fully integrated cell and gene therapy cGMP manufacturing facility served as the manufacturing site for PZ-Cel used in its Phase 3 VIITAL™ trial and is capable of supporting commercial production of PZ-Cel upon FDA approval. The company’s development portfolio also features AAV-based gene therapies for ophthalmic diseases with high unmet medical need. Abeona’s novel, next-generation AAV capsids are being evaluated to improve tropism profiles for a variety of devastating diseases.